FDA approves cure for sickle cell disease, the first ... - NBC News
WEBDec 8, 2023 · The Food and Drug Administration on Friday approved a powerful treatment for sickle cell disease, a devastating illness that affects more than 100,000 Americans, the majority of whom are...
First Day of a ‘New Life’ for a Boy With Sickle Cell
WEB5 days ago · Kendric Cromer undergoing infusion gene therapy for his sickle cell disease at Children’s National Hospital in Washington last week. ... Then the family got good news — Bluebird had completed ...
First Patient Begins Newly Approved Sickle Cell Gene Therapy
WEBMay 6, 2024 · On Wednesday, Kendric Cromer, a 12-year-old boy from a suburb of Washington, became the first person in the world with sickle cell disease to begin a commercially approved gene therapy that...
FDA approves first genetic treatments for sickle cell disease : …
WEBDec 8, 2023 · The Food and Drug Administration approved two genetic treatments for sickle cell disease, including one that uses gene-editing. The approvals offer hope for patients and signal a new...
Doctors cured her sickle-cell disease. So why is she still in pain?
WEB4 days ago · Sickle-cell disease is caused by a mutation in the gene encoding a component of haemoglobin, the oxygen-carrying protein complex found in red blood cells. ... An essential round-up of science news ...
FDA Approves First Gene Therapies to Treat Patients with Sickle Cell ...
WEBThe FDA has approved two cell-based gene therapies, Casgevy and Lyfgenia, to treat patients with sickle cell disease and reduce vaso-occlusive events. These therapies use genome editing or...
FDA approves two gene therapies for sickle cell, bringing hope to ... - CNN
WEBDec 8, 2023 · The medicines, called Casgevy and Lyfgenia, are potential cures for people with sickle cell, a debilitating and life-shortening inherited red blood cell disorder that disproportionately...
A Cure for Sickle Cell Disease | Johns Hopkins Medicine
WEBDec 12, 2023 · A national trial of low-dose haploidentical bone marrow transplant found it to be safe and curative for adults with severe sickle cell disease. The treatment does not require matched donors and has low side effects, according to the study presented at ASH.
The road to FDA approval for CRISPR gene-editing for sickle cell ...
WEBDec 25, 2023 · In early December, the Food and Drug Administration approved a gene-editing treatment for sickle cell disease, the first for any illness. One patient helped pave the way.
F.D.A. Approves 2 Sickle Cell Treatments, One ... - The New York Times
WEBDec 8, 2023 · On Friday, the Food and Drug Administration approved the first gene editing therapy ever to be used in humans, for sickle cell disease, a debilitating blood disorder caused by a single mutated...