Beta thalassemia is an inherited (genetic) disorder that affects 1.5% people worldwide. It is most common in people with ...

Genetic variability and sex-specific differences may play ... genotype, 7 had hemoglobin S beta thalassemia genotype, and 3 ...

During this investigation 3 children were found who had α-β-thalassemia disease, a condition not previously described in the Negro. The hematologic and genetic findings of this family and of ...

Beta-thalassemia is a rare blood disorder caused by a genetic defect in hemoglobin. Several manufacturers are developing novel treatments for the disease, including Vertex, which has partnered ...

Hemoglobin S–beta-thalassemia: When individuals are diagnosed with this form of sickle cell disease, they inherit one sickle cell gene from one parent and one gene for beta thalassemia from another ...

Casgevy is a gene-editing therapy which could be a game changer for CRISPR's business. The one-time treatment for sickle cell ...

In a world first, medical regulators in the UK have approved a gene therapy that aims to cure two blood disorders. The treatment for sickle cell disease and beta thalassemia is the first to be ...

Subtypes of alpha thalassemia are determined based on how many alpha globin genes are deleted. They include: Mutations in the HBB gene, which produces beta globin proteins, cause beta thalassemia.

this therapy treats sickle cell disease and transfusion-dependent beta thalassemia. Both are rare, debilitating blood ...

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CRISPR Therapeutics' first therapy is called Casgevy. It treats sickle cell disease (SCD) and beta thalassemia, both rare ...